Research & Development

The approval of Bluebird bio's gene therapy, Skysona, in September 2022 by the FDA marked a significant milestone for treating cerebral adrenoleukodystrophy (CALD), a rare and fatal childhood brain disorder. Skysona's innovation generated hope for families dealing with CALD, yet recent

In a dynamic twist within the pharmaceutical industry, several companies are locked in a fierce race to develop the next generation of obesity drugs. As the battle heats up, each aims to outdo the other, with innovations that promise to revolutionize the way obesity is treated. This race isn't

The biopharmaceutical industry is rapidly evolving, fueled by cutting-edge technologies and scientific breakthroughs. Novel treatments such as cell and gene therapies, biologics, and vaccines are reaching the market at unprecedented speeds. However, the rigorous journey from drug development to

Oculopharyngeal Muscular Dystrophy (OPMD) is a rare, progressive muscle-wasting disease that significantly impacts patients' quality of life. Limited therapeutic options are available, with current treatments failing to address the underlying muscle weakness driving the disease's

In an ambitious endeavor to revolutionize cancer treatment, Boehringer Ingelheim and Circle Pharma have entered into a research partnership and license agreement aimed at developing a first-in-class cyclin inhibitor. This groundbreaking collaboration is set to provide novel treatment options for

Innovation in biotechnology, particularly within the realm of cell therapy, hinges significantly on the expertise of regulatory professionals. These experts are instrumental in navigating complex regulatory landscapes and ensuring that scientific advances transition into viable, market-ready