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FDA approves two cell-based gene therapies for sickle cell disease

December 11, 2023


Affecting approximately 100,000 people in the US, SCD is a life-long, genetic disease that causes red blood cells to take a distinct crescent shape, which can block blood vessels and affect the way oxygen is carried around the body.

The disease can cause serious health problems, including severe pain and organ damage called vaso-occlusive events (VOEs) or vaso-occlusive crises (VOCs).

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