Rett syndrome is a severe neurological disorder primarily affecting young girls, leading to significant cognitive, motor, and communication impairments. The disorder is linked to mutations in the MeCP2 gene, which encodes the methyl-CpG binding protein 2 (MeCP2). Researchers have long sought to
A drug initially celebrated for its potential in treating a rare liver disease has come under scrutiny following alarming safety findings. Ocaliva, developed by Intercept Pharmaceuticals and now under Alfasigma's ownership, was initially viewed as a breakthrough treatment for primary biliary
The recent endorsement of Neuraxpharm's ublituximab (BRIUMVI®) by the National Institute for Health and Care Excellence (NICE) marks a significant step forward in the treatment of relapsing-remitting multiple sclerosis (RRMS). This approval is a notable accomplishment for the European
The recent endorsement by the National Institute for Health and Care Excellence (NICE) to utilize AstraZeneca's Imfinzi (durvalumab) in combination with chemotherapy as a treatment for adults with resectable non-small cell lung cancer (NSCLC) marks a significant milestone in cancer care. This
In a significant breakthrough, Poolbeg Pharma announced positive pre-clinical study results for their drug POLB 001, presented at the 66th American Society of Hematology (ASH) Annual Meeting. The study focused on the drug's potential to prevent Cytokine Release Syndrome (CRS), a frequently
The Keck School of Medicine of USC has embarked on a groundbreaking research initiative aimed at addressing age-related cognitive decline in women. This significant effort is led by Dr. Young-Kwon Hong and has been bolstered by securing a $3.4 million federal grant from the Advanced Research
