Tag: Amicus


CHMP backs Amicus’ therapy for Pompe disease

December 19, 2022

Via: Pharmaphorum

The CHMP said late last week it was recommending Pombiliti (cipaglucosidase alfa or ATB200) as an infused therapy for late-onset Pompe disease in adults given in combination with the enzyme stabiliser miglustat in a regimen known as AT-GAA. It’s the […]