Tag: ADA gene

Cell and Gene Therapy, Industry

Gene therapy successfully treats rare immunodeficiency in paediatric patients

May 12, 2021

Via: European Pharmaceutical Review

An experimental gene therapy developed by researchers at the US’s University of California – Los Angeles (UCLA) and UK’s Great Ormond Street Hospital (GOSH) in London has successfully treated 48 of 50 children born with a rare and deadly inherited […]